Larimar Publications
articles
- June 2025 | Pharmacokinetics and Pharmacodynamics of Nomlabofusp in Non‑clinical Studies of Friedreich’s Ataxia >
The AAPS Journal - March 2025 | Nomlabofusp, a Fusion Protein of Human Frataxin and a Cell Penetrant Peptide, Delivers Mature and Functional Frataxin into Mitochondria >
The AAPS Journal - November 2023 | Safety, pharmacokinetics, and pharmacodynamics of nomlabofusp (CTI-1601) in Friedreich’s ataxia >
Annals of Clinical and Translational Neurology
POSTERs
- November 2024 | Disease characteristics and tissue frataxin concentrations in adults with Friedreich’s ataxia participating in nomlabofusp interventional studies >
International Congress for Ataxia Research, London, UK- Encore presentations:
- March 2025 I American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting, Los Angeles, CA
- March 2025 I Muscular Dystrophy Clinical & Scientific Conference, Dallas, TX
- Encore presentations:
- November 2024 | Effect of nomlabofusp administration on tissue frataxin levels, plasma lipid profiles, and gene expression in patients with Friedreich’s ataxia >
International Congress for Ataxia Research, London, UK- Encore presentation:
- March 2025 I Muscular Dystrophy Clinical & Scientific Conference, Dallas, TX
- Encore presentation:
- November 2024 | Prediction of tissue frataxin levels with long term administration of nomlabofusp in adults with Friedreich’s ataxia using modeling and simulations >
International Congress for Ataxia Research, London, UK- Encore presentations:
- March 2025 I American College of Medical Genetics and Genomics (ACMG) Annual Clinical Genetics Meeting, Los Angeles, CA
- March 2025 I Muscular Dystrophy Clinical & Scientific Conference, Dallas, TX
- Encore presentations:
Related Publications
Larimar did not sponsor the publications listed below and is including them for informational purposes only.
articles
- March 2012 | A TAT–Frataxin fusion protein increases lifespan and cardiac function in a conditional Friedreich’s ataxia mouse model >
Human Molecular Genetics - March 2011 | Cardiomyopathy of Friedreich’s Ataxia Use of Mouse Models to Understand Human Disease and Guide Therapeutic Development >
Pediatric Cardiology - December 2010 | A rapid, noninvasive immunoassay for frataxin: Utility in assessment of Friedreich ataxia >
Molecular Genetics and Metabolism